Research and development of pharmaceuticals for the treatment of rare diseases; research and development for the treatment of hypertension, kidney stones, gallstones, cholesterol, rage disorders, lactation, schizophrenia, autism, kidney disease, neurodegeneration, infantile spasms, nephrotic syndrome, muscular dystrophy, and diabetic nephropathy

Pharmaceutical preparations for the treatment of liver disease and monogenic disease; pharmaceutical preparations for the treatment of disease, namely, kidney disease, metabolic disorders, or central nervous system disorders

Research and development of pharmaceuticals for the treatment of rare diseases; research and development for the treatment of hypertension, kidney stones, gallstones, cholesterol, rage disorders, lactation, schizophrenia, autism, kidney disease, neurodegeneration, infantile spasms, nephrotic syndrome, muscular dystrophy, and diabetic nephropathy

Pharmaceutical preparations for the treatment of liver disease and monogenic disease; pharmaceutical preparations for the treatment of disease, namely, kidney disease, metabolic disorders, or central nervous system disorders

Research and development of pharmaceuticals for the treatment of rare diseases; research and development for the treatment of hypertension, kidney stones, gallstones, cholesterol, rage disorders, lactation, schizophrenia, autism, kidney disease, neurodegeneration, infantile spasms, nephrotic syndrome, muscular dystrophy, and diabetic nephropathy

Pharmaceutical preparations for the treatment of liver disease and monogenic disease; pharmaceutical preparations for the treatment of disease, namely, kidney disease, metabolic disorders, or central nervous system disorders

Pharmaceutical preparations for the treatment of liver disease and monogenic disease; pharmaceutical preparations for the treatment of disease, namely, kidney disease, metabolic disorders, or central nervous system disorders

Pharmaceutical preparations for the treatment of liver disease and monogenic disease; pharmaceutical preparations for the treatment of disease, namely, kidney disease, metabolic disorders, or central nervous system disorders

Research and development of pharmaceuticals for the treatment of rare diseases;research and development for the treatment of hypertension, kidney stones, gallstones, cholesterol, rage disorders, lactation, schizophrenia, autism, kidney disease, neurodegeneration, infantile spasms, nephrotic syndrome, muscular dystrophy, and diabetic nephropathy

Pharmaceutical preparations for the treatment of catastrophic diseases, namely, focal segmental glomerulosclerosis, pantothenate kinase-associated neurodegeneration, duchenne muscular dystrophy and spinal muscular atrophy

Pharmaceutical preparations for the treatment of catastrophic diseases, namely, focal segmental glomerulosclerosis, pantothenate kinase-associated neurodegeneration, duchenne muscular dystrophy and spinal muscular atrophy