Pharmaceutical preparations for gene therapy and gene modulation; pharmaceutical compositions and therapeutic products in the nature of chemical and biological small molecules to degrade RNA, enhance expression, induce exon skipping, and rescue genetic lesions; pharmaceutical preparations, namely, RNA therapeutics for the treatment of genetic disorders, immune system related diseases and disorders, metabolic diseases and disorders, hematological diseases and disorders, cancer, neurological di...

pharmaceutical and therapeutic preparations for the treatment of cancer, immune system related diseases and disorders, cardiovascular diseases and disorders, genetic diseases and disorders, and neurological diseases and disorders