Pharmaceutical preparations for lysosomal storage disorders

Pharmaceutical preparations for the treatment of adult patients with mild to moderate type 1 Gaucher disease for whom enzyme replacement therapy is not a therapeutic option due to allergy, hypersensitivity, or poor venous access; Therapeutic pharmaceutical for the treatment of adult patients with mild to moderate type 1 Gaucher disease for whom enzyme replacement therapy is not a therapeutic option due to allergy, hypersensitivity, or poor venous access