Providing medical services in the field of genetic, central nervous system, and lysosomal storage diseases and disorders; medical consulting services in the field of genetic, central nervous system, and lysosomal storage diseases and disorders; healthcare services, namely, providing an online database of medical and healthcare information in the field of genetic, central nervous system, and lysosomal storage diseases and disorders, and collecting data and information on genetic, central nervo...

Pharmaceutical, scientific, and medical research and development in the field of genetic, central nervous system, and lysosomal storage diseases and disorders; scientific research in the nature of conducting clinical trials for others in the field of genetic, central nervous system, and lysosomal storage diseases and disorders; scientific and medical research, namely, compiling and sharing of patient data for research purposes in the field of genetic, central nervous system, and lysosomal sto...

Pharmaceutical preparations for the treatment of genetic, central nervous system, and lysosomal storage diseases and disorders; gene therapy products for the treatment of genetic, central nervous system, and lysosomal storage diseases and disorders, namely, virus vector-based gene therapies for intravenous delivery